Summary
Othera Pharmaceuticals, Inc. announced positive interim data results from its Phase 2 trial of OT-551 in treating geographic atrophy (GA) in dry AMD. OT-551 is a topically-dosed, patented small molecule that acts on oxidative stress and disease-induced inflammation. The 12-month findings from the two-year trial suggest an emerging trend for reducing moderate vision loss in 137 patients with GA who were treated with OT-551 compared with placebo.
Analysis
This topical eye drop for dry AMD is exciting for two reasons:
1) There are no treatments for treating Geographic Atrophy. The AREDs vitamins supplement are effective at preventing choroidal neovascularization but not geographic atrophy. The promising Phase II results would address a large unmet need in Macular Degeneration. All of the recent work has been on wet AMD.
2) It also shows that a topical formulation could be effective in treating posterior segment/retinal diseases. Dry AMD is a huge area where are not many treatments available. A topical formulation could be a blockbluster.
The actual results will be released in a few weeks at the ARVO meeting. It will be interesting to see what they show.


